PTC Therapeutics, Inc. today reported positive topline results from the 24-month interim analysis of the PIVOT-HD long-term extension study, with favorable dose-dependent effects on disease ...

PTC Therapeutics, Inc. will host a webcast conference call today, April 28 at 4:30 p.m. ET to share results from the 24-month interim analysis of the PIVOT-HD long-term extension study of votoplam.

Duchenne muscular dystrophy (DMD) is a genetic disease that causes progressive muscle weakness. DMD commonly affects boys, where symptoms are seen in early childhood. There is currently no cure for ...

Join us Friday, April 24, 2026. “Celebrating Collaborations: Students and Faculty Working Together” showcases the scholarly work of Smith College students across disciplines. From data sciences to art ...

A drug infusion is hardly dramatic, especially for a kid like 12-year-old Brecken Kinney, who has been poked and prodded his ...